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Author: Niyati Arora

Casgevy: A Year of Transformative Gene Therapy and Expanding Hope

December 2025 Update: From Breakthrough to Real-World Impact It’s been an incredible journey since the U.S. FDA made history by approving Vertex and CRISPR Therapeutics’ gene-editing therapy, Casgevy (exagamglogene autotemcel), for both Sickle Cell Disease (SCD) and Beta Thalassemia. What began as a monumental scientific

The Season of Giving is a Season of Hope

As we approach the end of the year, our thoughts naturally turn toward generosity, gratitude, and family. It’s the season of giving. But for many, the greatest gift isn’t something wrapped under a tree, it is the gift of hope. 🎄 For individuals living with thalassemia, hope
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